Clinical trials
Rare Diseases trials in Australia
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
11 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 1 |
| 2013 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 2 |
| 2025 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 3 |
| Completed | 2 |
| Terminated | 2 |
| Enrolling by invitation | 1 |
| Active, not recruiting | 1 |
| Unknown status | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Novartis Pharmaceuticals | 3 |
| Friedreich's Ataxia Research Alliance | 2 |
| AstraZeneca | 1 |
| Murdoch Childrens Research Institute | 1 |
| National Center for Research Resources (NCRR) | 1 |
| Prof. Valérie Mc Lin | 1 |
| Sanford Health | 1 |
| Swedish Orphan Biovitrum | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 11 |
| Friedreich Ataxia | 3 |
| Neurodegenerative Diseases | 3 |
| Ataxia | 2 |
| Huntington Disease | 2 |
| Addison Disease | 1 |
| Alagille Syndrome | 1 |
| Alstrom Syndrome | 1 |
| Amnesia, Transient Global | 1 |
| Aniridia | 1 |
Trials
Showing 1 to 11 of 11. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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