Clinical trials
Rare Diseases trials in France
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
59 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 2 |
| 2006 | 3 |
| 2009 | 1 |
| 2010 | 2 |
| 2013 | 2 |
| 2014 | 1 |
| 2015 | 3 |
| 2016 | 2 |
| 2017 | 3 |
| 2018 | 2 |
| 2019 | 3 |
| 2020 | 3 |
| 2021 | 5 |
| 2022 | 4 |
| 2023 | 6 |
| 2024 | 6 |
| 2025 | 4 |
| 2026 | 6 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 22 |
| Recruiting | 21 |
| Unknown status | 6 |
| Terminated | 3 |
| Not yet recruiting | 3 |
| Withdrawn | 2 |
| Enrolling by invitation | 1 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Assistance Publique - Hôpitaux de Paris | 10 |
| Institut National de la Santé Et de la Recherche Médicale, France | 7 |
| Imagine Institute | 6 |
| Amgen | 3 |
| Assistance Publique Hopitaux De Marseille | 2 |
| Associazione Angela Serra per la ricerca sul cancro | 2 |
| Centre Hospitalier Universitaire Dijon | 2 |
| Hospices Civils de Lyon | 2 |
| Laboratoire français de Fractionnement et de Biotechnologies | 2 |
| Novartis Pharmaceuticals | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 59 |
| Intellectual Disability | 5 |
| Genetic Diseases, Inborn | 4 |
| Metabolic Diseases | 4 |
| Cystinosis | 3 |
| Neurodegenerative Diseases | 3 |
| Polyradiculoneuropathy, Chronic Inflammatory Demyelinating | 3 |
| Arthritis, Juvenile | 2 |
| Autism Spectrum Disorder | 2 |
| Autoimmune Diseases | 2 |
Trials
Showing 1 to 25 of 59. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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