Clinical trials
Observational Rare Diseases trials in France
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
30 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 2 |
| 2006 | 1 |
| 2013 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 3 |
| 2018 | 1 |
| 2019 | 2 |
| 2020 | 1 |
| 2021 | 4 |
| 2022 | 1 |
| 2023 | 2 |
| 2024 | 5 |
| 2025 | 3 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 12 |
| Completed | 10 |
| Unknown status | 3 |
| Not yet recruiting | 2 |
| Enrolling by invitation | 1 |
| Terminated | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Assistance Publique - Hôpitaux de Paris | 8 |
| Imagine Institute | 6 |
| Institut National de la Santé Et de la Recherche Médicale, France | 4 |
| Associazione Angela Serra per la ricerca sul cancro | 2 |
| University Hospital, Strasbourg, France | 2 |
| Centre Hospitalier Universitaire Dijon | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| Hospices Civils de Lyon | 1 |
| NightstaRx Ltd, a Biogen Company | 1 |
| Orthofix s.r.l. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 30 |
| Genetic Diseases, Inborn | 3 |
| Intellectual Disability | 3 |
| Autism Spectrum Disorder | 2 |
| Autoimmune Diseases | 2 |
| Hypertension, Pulmonary | 2 |
| Neurodevelopmental Disorders | 2 |
| Neurologic Manifestations | 2 |
| Albinism | 1 |
| Antiphospholipid Syndrome | 1 |
Trials
Showing 1 to 25 of 30. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.