Skip to content

Clinical trials

Observational Rare Diseases trials in France

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Rare Diseases Phase: Observational Country / region: France Clear all

30 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20032
20061
20131
20151
20161
20173
20181
20192
20201
20214
20221
20232
20245
20253
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting12
Completed10
Unknown status3
Not yet recruiting2
Enrolling by invitation1
Terminated1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Assistance Publique - Hôpitaux de Paris8
Imagine Institute6
Institut National de la Santé Et de la Recherche Médicale, France4
Associazione Angela Serra per la ricerca sul cancro2
University Hospital, Strasbourg, France2
Centre Hospitalier Universitaire Dijon1
Friedreich's Ataxia Research Alliance1
Hospices Civils de Lyon1
NightstaRx Ltd, a Biogen Company1
Orthofix s.r.l.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Rare Diseases30
Genetic Diseases, Inborn3
Intellectual Disability3
Autism Spectrum Disorder2
Autoimmune Diseases2
Hypertension, Pulmonary2
Neurodevelopmental Disorders2
Neurologic Manifestations2
Albinism1
Antiphospholipid Syndrome1

Trials

Showing 1 to 25 of 30. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.