Clinical trials
Completed Rare Diseases trials in France
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
22 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 2 |
| 2006 | 3 |
| 2009 | 1 |
| 2010 | 2 |
| 2013 | 2 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2019 | 1 |
| 2020 | 1 |
| 2021 | 2 |
| 2022 | 2 |
| 2024 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 22 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amgen | 3 |
| Assistance Publique - Hôpitaux de Paris | 3 |
| Associazione Angela Serra per la ricerca sul cancro | 2 |
| Imagine Institute | 2 |
| Institut National de la Santé Et de la Recherche Médicale, France | 2 |
| Centre Hospitalier Universitaire Dijon | 1 |
| Genethon | 1 |
| Laboratoire français de Fractionnement et de Biotechnologies | 1 |
| NightstaRx Ltd, a Biogen Company | 1 |
| Novartis Pharmaceuticals | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 22 |
| Cystinosis | 3 |
| Metabolic Diseases | 2 |
| Acute Chest Syndrome | 1 |
| Anemia | 1 |
| Anemia, Sickle Cell | 1 |
| Arthritis, Juvenile | 1 |
| Bardet-Biedl Syndrome | 1 |
| Disease | 1 |
| Huntington Disease | 1 |
Trials
Showing 1 to 22 of 22. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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