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Clinical trials

Recruiting Rare Diseases trials in France

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Rare Diseases Status: Recruiting Country / region: France Clear all

21 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20161
20172
20191
20201
20221
20234
20244
20254
20263

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting21

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Institut National de la Santé Et de la Recherche Médicale, France4
Assistance Publique - Hôpitaux de Paris3
Imagine Institute3
University Hospital, Lille2
Assistance Publique Hopitaux De Marseille1
Centre Chirurgical Marie Lannelongue1
Centre Hospitalier Universitaire Dijon1
Friedreich's Ataxia Research Alliance1
Hospices Civils de Lyon1
Kyowa Kirin Co., Ltd.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Rare Diseases21
Genetic Diseases, Inborn3
Intellectual Disability2
Kidney Diseases2
Metabolic Diseases2
Neurologic Manifestations2
Arthritis, Juvenile1
Ataxia1
Autism Spectrum Disorder1
Autoimmune Diseases1

Trials

Showing 1 to 21 of 21. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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