Clinical trials
Rare Diseases trials in Italy
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
50 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2003 | 1 |
| 2006 | 1 |
| 2013 | 3 |
| 2015 | 2 |
| 2016 | 1 |
| 2018 | 3 |
| 2019 | 1 |
| 2020 | 1 |
| 2021 | 5 |
| 2022 | 2 |
| 2023 | 14 |
| 2024 | 5 |
| 2025 | 8 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 16 |
| Recruiting | 14 |
| Active, not recruiting | 7 |
| Unknown status | 5 |
| Terminated | 4 |
| Enrolling by invitation | 2 |
| Withdrawn | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| IRCCS Policlinico S. Donato | 10 |
| Associazione Angela Serra per la ricerca sul cancro | 3 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 3 |
| Istituto Ortopedico Rizzoli | 3 |
| Novartis Pharmaceuticals | 3 |
| Friedreich's Ataxia Research Alliance | 2 |
| Istituti Clinici Scientifici Maugeri SpA | 2 |
| Laboratoire français de Fractionnement et de Biotechnologies | 2 |
| Amgen | 1 |
| AstraZeneca | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 50 |
| Marfan Syndrome | 6 |
| Genetic Diseases, Inborn | 5 |
| Aortic Aneurysm, Thoracic | 3 |
| Friedreich Ataxia | 3 |
| Huntington Disease | 3 |
| Neurodegenerative Diseases | 3 |
| Peripheral Nervous System Diseases | 3 |
| Angioedemas, Hereditary | 2 |
| Cardiovascular Diseases | 2 |
Trials
Showing 1 to 25 of 50. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.