Clinical trials
Observational Rare Diseases trials in Italy
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
30 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2006 | 1 |
| 2018 | 3 |
| 2019 | 1 |
| 2020 | 1 |
| 2021 | 4 |
| 2022 | 1 |
| 2023 | 12 |
| 2024 | 2 |
| 2025 | 4 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 11 |
| Completed | 8 |
| Active, not recruiting | 4 |
| Unknown status | 4 |
| Enrolling by invitation | 2 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| IRCCS Policlinico S. Donato | 10 |
| Associazione Angela Serra per la ricerca sul cancro | 3 |
| Friedreich's Ataxia Research Alliance | 2 |
| Istituti Clinici Scientifici Maugeri SpA | 2 |
| CNAO National Center of Oncological Hadrontherapy | 1 |
| FROM- Fondazione per la Ricerca Ospedale di Bergamo- ETS | 1 |
| Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta | 1 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 1 |
| IRCCS Azienda Ospedaliero-Universitaria di Bologna | 1 |
| IRCCS Eugenio Medea | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 30 |
| Marfan Syndrome | 6 |
| Aortic Aneurysm, Thoracic | 3 |
| Genetic Diseases, Inborn | 3 |
| Angioedemas, Hereditary | 2 |
| Ehlers-Danlos Syndrome | 2 |
| Fatigue | 2 |
| Friedreich Ataxia | 2 |
| Leukoencephalopathies | 2 |
| Lymphoma, T-Cell, Peripheral | 2 |
Trials
Showing 1 to 25 of 30. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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