Clinical trials
Observational Rare Diseases trials in the Netherlands
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
4 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2023 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 1 |
| Enrolling by invitation | 1 |
| Recruiting | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Friedreich's Ataxia Research Alliance | 1 |
| NightstaRx Ltd, a Biogen Company | 1 |
| Prof. Valérie Mc Lin | 1 |
| REGENXBIO Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 4 |
| Genetic Diseases, Inborn | 2 |
| Ataxia | 1 |
| Atherosclerosis | 1 |
| Cardiovascular Diseases | 1 |
| Congenital Portosystemic Shunt | 1 |
| Friedreich Ataxia | 1 |
| Hepatic Encephalopathy | 1 |
| Hepatopulmonary Syndrome | 1 |
| Homozygous Familial Hypercholesterolemia | 1 |
Trials
Showing 1 to 4 of 4. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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