Clinical trials
Phase 2 Rare Diseases trials in the United Kingdom
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2016 | 1 |
| 2022 | 1 |
| 2023 | 2 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 3 |
| Active, not recruiting | 1 |
| Recruiting | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Novartis Pharmaceuticals | 2 |
| Boston University | 1 |
| RWTH Aachen University | 1 |
| Sanifit Therapeutics S. A. | 1 |
| Shionogi | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 6 |
| Huntington Disease | 2 |
| Neurodegenerative Diseases | 2 |
| Calcinosis | 1 |
| Calciphylaxis | 1 |
| Calcium Metabolism Disorders | 1 |
| Friedreich Ataxia | 1 |
| Genetic Diseases, Inborn | 1 |
| Glycogen Storage Disease | 1 |
| Glycogen Storage Disease Type II | 1 |
Trials
Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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