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Clinical trials

Terminated Rare Diseases trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Rare Diseases Status: Terminated Country / region: United States Clear all

15 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20002
20011
20131
20162
20182
20211

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated15

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
National Center for Research Resources (NCRR)3
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)2
AstraZeneca1
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)1
Fairview University Medical Center1
Gradalis, Inc.1
Hugo W. Moser Research Institute at Kennedy Krieger, Inc.1
Massachusetts General Hospital1
Novartis Pharmaceuticals1
Prisma Health-Upstate1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Rare Diseases15
Genetic Diseases, Inborn4
Respiratory Tract Diseases3
Communicable Diseases2
Immune System Diseases2
Neoplasms2
Urogenital Diseases2
Adrenoleukodystrophy1
Atherosclerosis1
Autistic Disorder1

Trials

Showing 1 to 15 of 15. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

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