Clinical trials
Enrolling by invitation Rare Diseases trials with no applicable phase
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
1 trial matches Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Enrolling by invitation | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Children's National Research Institute | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Anxiety Disorders | 1 |
| CHARGE Syndrome | 1 |
| Cockayne Syndrome | 1 |
| Factor VII Deficiency | 1 |
| Hemophilia A | 1 |
| Hernias, Diaphragmatic, Congenital | 1 |
| Noonan Syndrome | 1 |
| Rare Diseases | 1 |
| Short Bowel Syndrome | 1 |
| Trisomy 13 Syndrome | 1 |
Trials
Showing 1 to 1 of 1. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.