Clinical trials
Recruiting Rare Diseases trials with no applicable phase
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
15 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2018 | 1 |
| 2020 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 2 |
| 2024 | 3 |
| 2025 | 3 |
| 2026 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 15 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| University Hospital, Lille | 2 |
| Assistance Publique Hopitaux De Marseille | 1 |
| Baylor College of Medicine | 1 |
| Case Western Reserve University | 1 |
| Centre Chirurgical Marie Lannelongue | 1 |
| Cliniques universitaires Saint-Luc- Université Catholique de Louvain | 1 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 1 |
| Institut National de la Santé Et de la Recherche Médicale, France | 1 |
| Medical University of Vienna | 1 |
| Peking Union Medical College Hospital | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 15 |
| Genetic Diseases, Inborn | 3 |
| Adrenoleukodystrophy | 1 |
| Calciphylaxis | 1 |
| Cardiovascular Diseases | 1 |
| Disease | 1 |
| Genetic Predisposition to Disease | 1 |
| Genetic Risk Score | 1 |
| Heart Defects, Congenital | 1 |
| Hernias, Diaphragmatic, Congenital | 1 |
Trials
Showing 1 to 15 of 15. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.