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Clinical trials

Withdrawn Observational Rare Diseases trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Rare Diseases Phase: Observational Status: Withdrawn Clear all

5 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20151
20161
20211
20252

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Withdrawn5

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Assistance Publique - Hôpitaux de Paris1
Friedreich's Ataxia Research Alliance1
Swedish Orphan Biovitrum1
University of Kentucky1
Xperiome1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Rare Diseases5
Anemia, Sickle Cell1
Antiphospholipid Syndrome1
Arthritis, Psoriatic1
Arthritis, Rheumatoid1
Cystic Fibrosis1
Fanconi Anemia1
Friedreich Ataxia1
Hemophilia A1
Hemophilia B1

Trials

Showing 1 to 5 of 5. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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