Clinical trials
Observational Niemann-Pick Disease, Type C trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
8 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2011 | 1 |
| 2015 | 1 |
| 2018 | 2 |
| 2020 | 1 |
| 2021 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 2 |
| Recruiting | 2 |
| Withdrawn | 2 |
| Active, not recruiting | 1 |
| Enrolling by invitation | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 2 |
| Albert Einstein College of Medicine | 1 |
| CENTOGENE GmbH Rostock | 1 |
| Mayo Clinic | 1 |
| Melbourne Health | 1 |
| RTI International | 1 |
| ZevraDenmark | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Niemann-Pick Disease, Type C | 8 |
| Lysosomal Storage Diseases | 4 |
| Fabry Disease | 2 |
| Gaucher Disease | 2 |
| Leukodystrophy, Metachromatic | 2 |
| Mucopolysaccharidosis II | 2 |
| Mucopolysaccharidosis III | 2 |
| Mucopolysaccharidosis IV | 2 |
| Mucopolysaccharidosis VI | 2 |
| Mucopolysaccharidosis VII | 2 |
Trials
Showing 1 to 8 of 8. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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