Clinical trials
Propionic Acidemia trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
23 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2007 | 1 |
| 2008 | 1 |
| 2010 | 1 |
| 2012 | 2 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 2 |
| 2019 | 2 |
| 2021 | 6 |
| 2022 | 2 |
| 2023 | 1 |
| 2024 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Recruiting | 7 |
| Terminated | 4 |
| Active, not recruiting | 1 |
| Not yet recruiting | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ModernaTX, Inc. | 4 |
| HemoShear Therapeutics | 2 |
| Mendel Tuchman | 2 |
| RECORDATI GROUP | 2 |
| Centre Hospitalier Universitaire de Liege | 1 |
| Children's Hospital of Philadelphia | 1 |
| CoA Therapeutics, Inc., a BridgeBio company | 1 |
| Emma Marie Caroline Slack | 1 |
| King Abdullah International Medical Research Center | 1 |
| Mayo Clinic | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Propionic Acidemia | 23 |
| Metabolism, Inborn Errors | 8 |
| Carbamoyl-Phosphate Synthase I Deficiency Disease | 5 |
| Metabolic Diseases | 5 |
| Genetic Diseases, Inborn | 4 |
| Hyperammonemia | 4 |
| Ornithine Carbamoyltransferase Deficiency Disease | 4 |
| Urea Cycle Disorders, Inborn | 4 |
| Argininosuccinic Aciduria | 3 |
| Citrullinemia | 3 |
Trials
Showing 1 to 23 of 23. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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