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Clinical trials

Completed Heredodegenerative Disorders, Nervous System trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Heredodegenerative Disorders, Nervous System Status: Completed Clear all

9 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20001
20112
20121
20191
20202
20221
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed9

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Siena Biotech S.p.A.2
State University of New York at Buffalo2
Alnylam Pharmaceuticals1
Avidity Biosciences, Inc.1
National Human Genome Research Institute (NHGRI)1
PepGen Inc1
University of South Florida1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Heredodegenerative Disorders, Nervous System9
Genetic Diseases, Inborn6
Nervous System Diseases5
Neurodegenerative Diseases5
Dementia3
Neuromuscular Diseases3
Basal Ganglia Diseases2
Brain Diseases2
Central Nervous System Diseases2
Chorea2

Trials

Showing 1 to 9 of 9. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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