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Clinical trials

Propionic Acidemia trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Propionic Acidemia Country / region: United States Clear all

16 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20071
20081
20122
20161
20171
20182
20215
20221
20231
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting6
Completed5
Terminated4
Active, not recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
ModernaTX, Inc.4
HemoShear Therapeutics2
Mendel Tuchman2
CoA Therapeutics, Inc., a BridgeBio company1
Mayo Clinic1
National Human Genome Research Institute (NHGRI)1
Nicola Longo1
RECORDATI GROUP1
RTI International1
University of Pittsburgh1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Propionic Acidemia16
Metabolism, Inborn Errors6
Metabolic Diseases5
Genetic Diseases, Inborn4
Hyperammonemia4
Carbamoyl-Phosphate Synthase I Deficiency Disease3
Ornithine Carbamoyltransferase Deficiency Disease3
Acid-Base Imbalance2
Acidosis2
Amino Acid Metabolism, Inborn Errors2

Trials

Showing 1 to 16 of 16. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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