Skip to content

Clinical trials

Observational Propionic Acidemia trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Propionic Acidemia Phase: Observational Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20161
20171
20182
20191
20212
20222
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed4
Recruiting4
Active, not recruiting1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
ModernaTX, Inc.2
RECORDATI GROUP2
Centre Hospitalier Universitaire de Liege1
Emma Marie Caroline Slack1
HemoShear Therapeutics1
National Human Genome Research Institute (NHGRI)1
RTI International1
University of Pittsburgh1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Propionic Acidemia10
Metabolism, Inborn Errors4
Anemia, Sickle Cell2
Argininosuccinic Aciduria2
Biotinidase Deficiency2
Carbamoyl-Phosphate Synthase I Deficiency Disease2
Citrullinemia2
Congenital Hyperinsulinism2
Congenital Hypothyroidism2
Cystic Fibrosis2

Trials

Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.